Exploratory Phase 2a study showed consistent and clinically meaningful functional improvements across muscle strength, motor performance, and patient-reported outcomes in patients with ...
NEW YORK, NEW YORK , UNITED STATES , January 10, 2024 /EINPresswire.com/ -- In partnership with InformedDNA ®, the Hereditary Neuropathy Foundation (HNF) has added ...
A phase 2a trial of NMD Pharma’s rare disease prospect ignaseclant has missed its primary endpoint. | A phase 2a trial of NMD ...
This review provides a concise overview of the epidemiology, etiology, history, diagnostic criteria, and management of Charcot-Marie-Tooth disease. Charcot-Marie-Tooth (CMT) disease is a group of ...
9-1-1: Nashville star Isabelle Tate’s death is bringing attention to a rare disease. On Thursday, October 23, news broke that the actress had died at the age of 23. Her agency confirmed the news via ...